Onasemnogene abeparvovec

Brand name: Zolgensma

D

Score D — Possible Hepatotoxin

Single case reports have appeared implicating this drug, but the evidence is limited.

Fewer than 3 cases have been reported in the literature. No characteristic signature has been identified, and the case reports may not have been very convincing.

Primary class Genetic
Secondary class Spinal Muscular Atrophy
FDA approval 2019